Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude Children’s Research Hospital led the first in utero treatment of SMA with ...

At its core, SMA is caused by a deficiency in a protein called Survival Motor Neuron (SMN) . This protein is essential for the health and survival of motor neurons—the nerve cells that sit in the ...

Spinal Muscular Atrophy companies are Amniotics, Biohaven Pharmaceuticals, Hoffmann-La Roche, Amylon Therapeutics, Voyager Therapeutics, Catalyst Pharmaceuticals ...

The SMA treatment team also includes rehabilitation professionals such as respiratory, physical, occupational, and speech therapists. Rehabilitation treatment involves care related to positioning, ...

In their first year of life, a baby typically learns to lift his head, roll over, crawl and perhaps even take his or her first steps. But for infants with spinal muscular atrophy (SMA), these ...

Spinal muscular atrophy (SMA) is a rare genetic condition that causes progressive muscle weakness, which, when untreated, prevents infants with the most severe form from gaining motor development — ...

The Key Spinal Muscular Atrophy Companies in the market include - Genentech, F. Hoffmann-La Roche, Scholar Rock, Biohaven/ Bristol-Myers Squibb, NMD Pharma, Novartis, Hoffmann-La Roche, Genentech, Inc ...

The baby from Ranaghat in Nadia is suffering from spinal muscular atrophy (SMA) Type I, a condition that causes progressive weakening of the muscles and nerves A 16-month-old girl with a rare genetic ...

The former Little Mix singer posted an emotional video to Instagram on Sunday, vowing that the girls will "fight all the odds ...

A community workshop titled “Kaikorthu – Together in KARE This New Year,” aimed at empowering the families of children affected by Spinal Muscular Atrophy (SMA), was organised on Friday at the CRC ...